๐Ÿ”ฅ The First Treatment for "Childhood Alzheimer's" Is One Shot โ€” and a $3.95 Million Bill

๐Ÿ”ฅ The First Treatment for "Childhood Alzheimer's" Is One Shot โ€” and a $3.95 Million Bill

The FDA just approved FAYUVI, the first-ever treatment for Sanfilippo syndrome type A: a one-time gene therapy from Ultragenyx priced at $3.95 million per patient.